[Advance in therapy for Duchenne/Becker muscular dystrophy]

Tian-Tian Xu1, Dan Lan

  • 1Department of Pediatrics, First Affiliated Hospital of Guangxi Medical University, Nanning 530021, China. land6785@163.com.

Summary

Duchenne/Becker muscular dystrophy (DMD/BMD), an inherited neuromuscular disease, involves progressive muscle weakness due to dystrophin gene mutations. Promising new therapies, including cell and gene therapy, are advancing treatment options for this condition.