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Discontinuation of enzyme replacement therapy in Fabry disease in the Dutch cohort

Maarten Arends1, Gabor E Linthorst1, Carla E Hollak1

  • 1Department of Internal Medicine, Division Endocrinology and Metabolism, Academic Medical Center, PO Box 22660, Amsterdam 1100 DD, The Netherlands.

Molecular Genetics and Metabolism
|December 15, 2015
PubMed

Keywords:
AgalsidaseDiscontinuationERTEnzyme replacement therapyFabry disease

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