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[Antioxidative therapy in ceroid lipofuscinosis]
1Interdisciplinair Kinderneurologisch Centrum, St. Radboudziekenhuis, Nijmegen.
Summary
Antioxidant therapy for ceroid lipofuscinoses (CLF) showed no effect in late-infantile forms but mitigated symptoms in juvenile CLF. This suggests antioxidant treatment for CLF is symptomatic, not curative.
Area of Science:
- Neuroscience
- Genetics
- Biochemistry