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Updated: Feb 26, 2026

Subretinal Injection of Gene Therapy Vectors and Stem Cells in the Perinatal Mouse Eye
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Published on: November 25, 2012

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Development of gene therapies-lessons from nusinersen

L Xu1, I Irony1, W W Bryan1

  • 1Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.

Gene Therapy
|July 25, 2017
PubMed

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