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Frataxin Restoration in the Nervous System: Possibilities for Gene Therapy

David R Lynch1, Elizabeth Kichula1, Hong Lin1

  • 1Division of Neurology, Children's Hospital of Philadelphia, 502 Abramson Research Center, 3615 Civic Center Boulevard, Philadelphia, PA 19104, USA.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|August 7, 2018
PubMed
Abstract

No abstract available in PubMed .

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