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Of mice and men: Plasma phenylalanine reduction in PKU corrects neurotransmitter pathways in the brain

Geoffrey Y Berguig1, Nathan T Martin1, Athena Y Creer1

  • 1BioMarin Pharmaceutical Inc., Novato, CA, USA.

Molecular Genetics and Metabolism
|October 26, 2019
PubMed

Keywords:
BiomarkersNeurotransmittersPKUPegvaliasePhenylketonuria

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