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Implementation of Non-invasive Point of Care Transient Elastography for Evaluation of Liver Disease in Pediatric Populations with Cystic Fibrosis
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Cystinosis: Therapy adherence and metabolic monitoring in patients treated with immediate-release cysteamine

Simone Linden1, Sabrina Klank1, Erik Harms1

  • 1Department of General Pediatrics, Metabolic Diseases, University Children's Hospital, Albert-Schweitzer-Campus 1, Münster, NRW DE 48149, Germany.

Molecular Genetics and Metabolism Reports
|July 21, 2020
PubMed
Abstract

Keywords:
AdherenceCysteamineCystine levelCystinosisMetabolic monitoring

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