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Updated: Dec 2, 2025

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Evaluation of Exon Inclusion Induced by Splice Switching Antisense Oligonucleotides in SMA Patient Fibroblasts
Published on: May 11, 2018
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Outcomes in type 1 spinal muscular atrophy on nusinersen: A single center experience
Joshua Kaltman1, Emily Kern-Smith2, Chao Zhang3
1Emory University School of Medicine, Atlanta, GA, USA.
Abstract
No abstract available in PubMed .
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