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Updated: Nov 19, 2025

CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications
Published on: August 9, 2022
Moyra Lawrence1,2, Annett Mueller1,2, Cedric Ghevaert1,2
1Department of Haematology, University of Cambridge and NHS Blood and Transplant, Long Road, Cambridge CB2 0PT, U.K.
Genome editing advances regenerative medicine by creating universal platelets through beta-2 microglobulin deletion. This ensures a stable, quality-controlled supply for patients needing transfusions.
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