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Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
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2020 Update to Spinal Muscular Atrophy Management in Saudi Arabia

Fahad A Bashiri1,2, Mohamad-Hani Temsah1,3, Khalid Hundallah4

  • 1College of Medicine, King Saud University, Riyadh, Saudi Arabia.

Frontiers in Pediatrics
|June 17, 2021
PubMed

Keywords:
Saudi Arabiagene therapynusinersenonasemnogene abeparvovecrisdiplamspinal muscular atrophy

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