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CRISPR/Cas9-mediated Targeted Integration In Vivo Using a Homology-mediated End Joining-based Strategy
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Published on: March 12, 2018

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In vivo delivery of CRISPR-Cas9 therapeutics: Progress and challenges

Matthew Behr1, Jing Zhou2, Bing Xu3

  • 1Department of Pharmaceutical Sciences, School of Pharmacy-Boston, Massachusetts College of Pharmacy and Health Sciences, Boston, MA 02115, USA.

Acta Pharmaceutica Sinica. B
|September 15, 2021
PubMed

Keywords:
AAVCRISPRCas9Genome editing therapyIn vivoLNPLentivirusNanoparticle

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