Author's Response to: Rebuttal to: Simvastatin Treatment Does Not Ameliorate Muscle Pathophysiology in a Mouse Model for Duchenne Muscular Dystrophy, Verhaart et al. 2020

Therapeutic oligonucleotides as genetic medicines: The current state and future perspective.

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A simplified and reproducible protocol for percutaneous lumbar intrathecal injection in rats.

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Four new mouse models of Duchenne muscular dystrophy with clinically relevant exon deletions in the human DMD gene.

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Individualized antisense oligonucleotide treatment eligibility of patients living with neurodevelopmental diseases.

Cell reports. Medicine·2026

Evaluating exon skipping in the central nervous system in Duchenne muscular dystrophy using spatial transcriptomics.

iScience·2026

Guidance on communication and informed consent with patients and their families for experimental individualized treatments.

American journal of human genetics·2026

Managing growth and puberty concerns in individuals with Duchenne muscular dystrophy: Updated guidance and future directions.

Journal of neuromuscular diseases·2026

Combined qualitative and quantitative MRI reveals short-term progression in facioscapulohumeral muscular dystrophy.

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An international patient survey of RYR1-related diseases: The patient perspective on clinical trial participation.

Journal of neuromuscular diseases·2026

Adrenal insufficiency in individuals with Duchenne muscular dystrophy treated with glucocorticoids: Insights from the past, current challenges, and future directions.

Journal of neuromuscular diseases·2026

Delving into the clinical and genetic spectrum of NLSDM: A case study.

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Cramps as the initial presentation of CANVAS/RFC1-related disorder.

Journal of neuromuscular diseases·2026

Tibial Plateau Fracture in a Patient with Fibular Hemimelia: A Case Report.

Journal of orthopaedic case reports·2026

Intraoperative Discovery of Incorrect Femoral Component Packaging during Bilateral Total Knee Arthroplasty: A Near-Miss Case Report.

Journal of orthopaedic case reports·2026

AR-V7 Utilizes a Noncanonical Nuclear Localization Signal to Sustain Androgen-Independent Nuclear Import and Signaling.

bioRxiv : the preprint server for biology·2026

Complete Discoid Medial Meniscus With Absent Anterior Horn Osseous Insertion Tethered by an Oblique Meniscomeniscal Ligament: A Case Report.

JBJS case connector·2026

Vertebral Artery Dissection and PICA-Territory Stroke Associated with Chronic Atlantoaxial Structural Abnormality: A Case Report.

Neurology international·2026

Limited Added Effect of Proline-Rich P6 Peptide to Cross-Linked Hyaluronic Acid After Partial Lateral Meniscectomy in Sheep.

Smart medicine·2026

Related Experiment Videos

Author's Response to: Rebuttal to: Simvastatin Treatment Does Not Ameliorate Muscle Pathophysiology in a Mouse Model

Related Concept Videos

Therapeutic oligonucleotides as genetic medicines: The current state and future perspective.

A simplified and reproducible protocol for percutaneous lumbar intrathecal injection in rats.

Four new mouse models of Duchenne muscular dystrophy with clinically relevant exon deletions in the human DMD gene.

Individualized antisense oligonucleotide treatment eligibility of patients living with neurodevelopmental diseases.

Evaluating exon skipping in the central nervous system in Duchenne muscular dystrophy using spatial transcriptomics.

Guidance on communication and informed consent with patients and their families for experimental individualized treatments.

Managing growth and puberty concerns in individuals with Duchenne muscular dystrophy: Updated guidance and future directions.

Combined qualitative and quantitative MRI reveals short-term progression in facioscapulohumeral muscular dystrophy.

An international patient survey of RYR1-related diseases: The patient perspective on clinical trial participation.

Adrenal insufficiency in individuals with Duchenne muscular dystrophy treated with glucocorticoids: Insights from the past, current challenges, and future directions.

Delving into the clinical and genetic spectrum of NLSDM: A case study.

Cramps as the initial presentation of CANVAS/RFC1-related disorder.

Tibial Plateau Fracture in a Patient with Fibular Hemimelia: A Case Report.

Intraoperative Discovery of Incorrect Femoral Component Packaging during Bilateral Total Knee Arthroplasty: A Near-Miss Case Report.

AR-V7 Utilizes a Noncanonical Nuclear Localization Signal to Sustain Androgen-Independent Nuclear Import and Signaling.

Complete Discoid Medial Meniscus With Absent Anterior Horn Osseous Insertion Tethered by an Oblique Meniscomeniscal Ligament: A Case Report.

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Related Experiment Videos

Author's Response to: Rebuttal to: Simvastatin Treatment Does Not Ameliorate Muscle Pathophysiology in a Mouse Model...

Related Concept Videos

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Author's Response to: Rebuttal to: Simvastatin Treatment Does Not Ameliorate Muscle Pathophysiology in a Mouse Model