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Updated: Oct 13, 2025

Generation of Native, Untagged Huntingtin Exon1 Monomer and Fibrils Using a SUMO Fusion Strategy
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Gene Therapy for Huntington's Disease: The Final Strategy for a Cure?

Seulgi Byun1,2, Mijung Lee1, Manho Kim1,3

  • 1Department of Neurology, Seoul National University Hospital, Seoul, Korea.

Journal of Movement Disorders
|November 16, 2021
PubMed

Keywords:
Gene transferHuntington’s diseaseMovement disorder

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