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Therapeutic Approaches in Lysosomal Storage Diseases

Carlos Fernández-Pereira1, Beatriz San Millán-Tejado1, María Gallardo-Gómez1

  • 1Rare Disease and Pediatric Medicine Group, Galicia Sur Health Research Institute (IIS Galicia Sur), SERGAS-UVIGO, 36312 Vigo, Spain.

Biomolecules
|December 24, 2021
PubMed

Keywords:
autophagyenzyme replacement therapygene therapylysosomal storage diseasessmall molecules

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