Related Experiment Video
Updated: Jul 30, 2025
10:16
In Vitro Enzyme Measurement to Test Pharmacological Chaperone Responsiveness in Fabry and Pompe Disease
Published on: December 20, 2017
8.1K
Medication adherence in Fabry patients treated with migalastat: Real world experience
Eleonora Riccio1, Oriana de Marco2, Antonio Pisani2
1Institute for Biomedical Research and Innovation, National Research Council of Italy (IRIB CNR), Palermo, Italy.
Molecular Genetics and Metabolism Reports
|May 14, 2023
Abstract
No abstract available in PubMed .
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