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Restoring Ciliary Function: Gene Therapeutics for Primary Ciliary Dyskinesia

Nicholas W Keiser1, Erin Cant2, Sneha Sitaraman1

  • 1Spirovant Sciences, Inc., Philadelphia, Pennsylvania, USA.

Human Gene Therapy
|August 25, 2023
PubMed

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Keywords:
AAVciliagene therapylungviral vectors