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Lentiviral Vector-mediated Gene Therapy of Hepatocytes Ex Vivo for Autologous Transplantation in Swine
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Liver gene transfer for metabolite detoxification in inherited metabolic diseases

Alfonso M D'Alessio1,2, Iolanda Boffa1,3, Lucia De Stefano1

  • 1Telethon Institute of Genetics and Medicine (TIGEM), Pozzuoli, Italy.

FEBS Letters
|June 17, 2024
PubMed

Keywords:
AAVgene therapyinherited metabolic disorderslipid nanoparticleslivermetabolite detoxification

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