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Induced Pluripotent Stem Cells and CRISPR-Cas9 Innovations for Treating Alpha-1 Antitrypsin Deficiency and Glycogen

Colin Walsh1, Sha Jin1

  • 1Department of Biomedical Engineering, Thomas J. Watson College of Engineering and Applied Sciences, State University of New York at Binghamton, Binghamton, NY 13902, USA.

Cells
|June 26, 2024
PubMed

Keywords:
CRISPR-Cas9alpha-1 antitrypsin deficiencygene therapyglycogen storage diseaseinduced pluripotent stem cellsmetabolic disorderstherapeutic modeling

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