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Updated: Jun 21, 2025

Evaluation of Exon Inclusion Induced by Splice Switching Antisense Oligonucleotides in SMA Patient Fibroblasts
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Gene therapy offers promise, but timing is crucial for SMA treatment

Renu Suthar1, Abhishek Pandey1, Prashant Jauhari2

  • 1Pediatric Neurology Unit, Department of Pediatrics, Post Graduate Institute of Medical Education & Research (PGIMER), Chandigarh, India.

European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society
|July 13, 2024
PubMed
Abstract

No abstract available in PubMed .

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