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Current approaches in CRISPR-Cas systems for hereditary diseases

Swati Singh1, Divakar Raj1, Ashish Mathur1

  • 1School of Health Sciences & Technology, UPES, Dehradun, Uttarakhand, India.

Progress in Molecular Biology and Translational Science
|January 17, 2025
PubMed
Summary

CRISPR-Cas gene editing offers a revolutionary approach to treating inherited disorders by precisely correcting disease-causing mutations. This technology holds promise for a wide range of genetic conditions, ushering in a new era of precision medicine.

Keywords:
Cas proteinCrisper cas9DNA editingDNA repairGenetic disorderGenome editing toolHereditary disease

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