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Home Enzyme Replacement Therapy in Gaucher Disease: A Review

Beata Kieć-Wilk1,2, Paul Guijt3, Michaela Dan4

  • 1Unit of Rare Metabolic Diseases, Department of Pathophysiology, Jagiellonian University Medical College, 31-121 Krakow, Poland.

Journal of Clinical Medicine
|February 13, 2025
PubMed

Keywords:
Gaucher diseasecomplianceenzyme replacement therapyhome therapysafety

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