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AAV-Based Gene Therapy: Opportunities, Risks, and Scale-Up Strategies

Daniil Moldavskii1, Zarema Gilazieva1, Alisa Fattakhova1

  • 1Institute of Fundamental Medicine and Biology, Kazan Federal University, Kazan 420008, Russia.

International Journal of Molecular Sciences
|September 13, 2025
PubMed
Abstract

Keywords:
AAV manufacturingAAV productiongene therapygene therapy vectorshigh-titer AAV

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