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Updated: Jan 17, 2026

Generation of Induced Pluripotent Stem Cells from Muscular Dystrophy Patients: Efficient Integration-free Reprogramming of Urine Derived Cells
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Pluripotent stem cell-based therapy toward the clinic for muscular dystrophy

Helena Escobar1

  • 1Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125 Berlin, Germany; Charité - Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Charité Campus Buch, 13125 Berlin, Germany; Muscle Research Unit, Experimental and Clinical Research Center (ECRC), a joint cooperation between the Charité - Universitätsmedizin Berlin and the Max Delbrück Center for Molecular Medicine in the Helmholtz Association (MDC), 13125 Berlin, Germany.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|September 23, 2025
PubMed
Summary

No abstract available in PubMed .

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