iRGD-engineered exosomes mediate siMYC delivery for effective tumor suppression in triple-negative breast cancer

Hui Li1, Weiguang Yuan2,3, Jialin Liu4,5,6

  • 1Department of Ultrasound, The First Affiliated Hospital of Harbin Medical University, Harbin, China.

Nanoscale
|December 12, 2025
PubMed

Insights

Engineered exosomes carrying therapeutic RNA effectively target and treat triple-negative breast cancer. This novel exosome delivery system enhances gene silencing and reduces tumor growth with minimal toxicity.

Area of Science:

  • Biomedical Engineering
  • Nanomedicine
  • Cancer Therapy

Background:

  • Triple-negative breast cancer (TNBC) is aggressive with limited treatment options.
  • MYC overexpression is a key driver of TNBC progression.
  • Efficient delivery of therapeutic agents like small interfering RNA (siRNA) against MYC is challenging.

Purpose of the Study:

  • To engineer exosomes modified with an internalizing RGD peptide (iRGD) for enhanced delivery of siMYC to TNBC cells.
  • To evaluate the therapeutic efficacy and biosafety of iRGD-exosomes loaded with siMYC (iRGD-Exos-siMYC) in preclinical models.

Main Methods:

  • Engineered exosomes (iRGD-Exos) by transfecting 293-F cells with an iRGD-Flag-Lamp2b plasmid.
  • Loaded siMYC into exosomes via electroporation.
  • Assessed exosome uptake, TNBC cell proliferation, apoptosis (in vitro and in patient-derived organoids), tumor targeting, and therapeutic effects in a TNBC xenograft mouse model.
  • Evaluated systemic toxicity through hematological, biochemical, and histopathological analyses.

Main Results:

  • iRGD modification significantly increased exosome uptake by TNBC cells expressing αvβ3 integrin.
  • iRGD-Exos-siMYC effectively suppressed TNBC cell proliferation and induced apoptosis in vitro and in patient-derived organoids.
  • In vivo studies demonstrated superior tumor targeting, significant tumor growth inhibition, and MYC expression downregulation.
  • Systemic toxicity assessments confirmed good biosafety of the engineered exosomes.

Conclusions:

  • iRGD-modified exosomes serve as an effective platform for delivering siMYC to TNBC cells, enhancing gene silencing and antitumor efficacy.
  • This targeted exosomal drug delivery system exhibits high tumor selectivity and minimal systemic toxicity.
  • iRGD-Exos-siMYC represents a promising novel therapeutic strategy for triple-negative breast cancer.