Recent Advances on RNA-Based Molecular Therapies for Tumour Cell Targeting

Navneet Sharma1, Akash Bhati1, Kamal Shah2

  • 1University Institute of Pharma Sciences (UIPS), Chandigarh University NH-05, Chandigarh, Ludhiana Highway, Mohali, Punjab, 140413, India.

Current Gene Therapy
|January 9, 2026
PubMed

Insights

RNA-based therapies offer targeted cancer treatment by exploiting genetic alterations. Research is advancing RNA delivery systems, nanoparticles, and AI for improved efficacy and reduced side effects in oncology.

Area of Science:

  • Oncology
  • Molecular Biology
  • Biotechnology

Background:

  • Anticancer drug development traditionally targets existing tumor cell genetic alterations.
  • Loss-of-function genetic screens identify genes crucial for tumor growth, cytotoxicity, and apoptosis.
  • RNA's emerging role in cancer diagnosis and therapy is a significant area of medical research.

Purpose of the Study:

  • To review RNA-based therapies for cancer treatment.
  • To discuss mechanisms of action, clinical applications, and advancements in RNA delivery systems.
  • To explore the integration of nanoparticles and artificial intelligence in tumor targeting.

Main Methods:

  • Summarization of current research on RNA-based therapies.
  • Analysis of various RNA types, including small interfering RNA (siRNA) and microRNA (miRNA).
  • Review of RNA delivery systems like exosomes and advancements in RNA tracking and stability.

Main Results:

  • Numerous mRNA and oligonucleotide drugs (ASOs, siRNAs, aptamers, miRNAs) are in clinical development pipelines.
  • Several RNA-based therapies have received clinical approval.
  • RNA therapies demonstrate high specificity and adaptability for cancer treatment.

Conclusions:

  • RNA-based therapies hold substantial promise for cancer treatment.
  • Continued research is essential to optimize delivery methods and minimize side effects.
  • Exploring novel RNA targets is critical for advancing these therapies into widespread clinical practice.

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