A mixed message for cystic fibrosis gene therapy

Effect and duration of lung volume reduction surgery: mid-term results of the Brompton trial.

The Thoracic and cardiovascular surgeon·2006

Improving rate of decline of FEV1 in young adults with cystic fibrosis.

Thorax·2005

Gene therapy progress and prospects: bringing gene therapy into medical practice: the evolution of international ethics and the regulatory environment.

Gene therapy·2004

Normal nasal mucociliary clearance in CF children: evidence against a CFTR-related defect.

The European respiratory journal·2004

Immunological hurdles to lung gene therapy.

Clinical and experimental immunology·2003

Management of influenza in patients with asthma or chronic obstructive pulmonary disease.

Annals of allergy, asthma & immunology : official publication of the American College of Allergy, Asthma, & Immunology·2002

Spatial analysis of head and neck cancer identifies two ecosystems with distinct modes of epithelial-to-mesenchymal transition.

Nature genetics·2026

PLCG2 downregulation impairs synaptic function and increases Alzheimer's disease hallmarks in neuronal cultures.

Nature genetics·2026

Correlations between causal effect sizes of proximal SNPs vary with functional annotations and implicate stabilizing selection.

Nature genetics·2026

hnRNPK condensates facilitate enhancer-promoter looping and RNA polymerase II recruitment.

Nature genetics·2026

Plasticity of human microglia and brain perivascular macrophages in aging and Alzheimer's disease.

Nature genetics·2026

Prevalence and chronology of colibactin-associated mutational processes and their microbiome spectra in Japanese colorectal cancer.

Nature genetics·2026

RETRACTION: Up-regulated Mir-192-5p Expression Rescues Cognitive Impairment and Restores Neural Function in Mice With Depression via the Fbln2 -mediated TGF-β1 Signaling Pathway.

FASEB journal : official publication of the Federation of American Societies for Experimental Biology·2026

Transferrin-Conjugated Polymeric Nanoparticles via Polymerization-Induced Self-Assembly for Enhanced BBB Transport and Glioblastoma Therapy.

ACS applied bio materials·2026

Dasatinib-Loaded Human Serum Albumin Nanoparticle-Impregnated Hydrogel for Localised Eradication of Residual Melanoma: Integrated In Silico, 3D Spheroid, and Dermatokinetic Evaluation.

ACS applied bio materials·2026

Therapeutic Advances and Biomarkers in Multiple Sclerosis.

Current neuropharmacology·2026

Phospholipid-modified glycogen nanoparticles for synergistic chemo-photothermal treatment of glioblastoma.

Nanoscale·2026

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTR.

Human gene therapy·2026

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A mixed message for cystic fibrosis gene therapy

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Effect and duration of lung volume reduction surgery: mid-term results of the Brompton trial.

Improving rate of decline of FEV1 in young adults with cystic fibrosis.

Gene therapy progress and prospects: bringing gene therapy into medical practice: the evolution of international ethics and the regulatory environment.

Normal nasal mucociliary clearance in CF children: evidence against a CFTR-related defect.

Immunological hurdles to lung gene therapy.

Management of influenza in patients with asthma or chronic obstructive pulmonary disease.

Spatial analysis of head and neck cancer identifies two ecosystems with distinct modes of epithelial-to-mesenchymal transition.

PLCG2 downregulation impairs synaptic function and increases Alzheimer's disease hallmarks in neuronal cultures.

Correlations between causal effect sizes of proximal SNPs vary with functional annotations and implicate stabilizing selection.

hnRNPK condensates facilitate enhancer-promoter looping and RNA polymerase II recruitment.

Plasticity of human microglia and brain perivascular macrophages in aging and Alzheimer's disease.

Prevalence and chronology of colibactin-associated mutational processes and their microbiome spectra in Japanese colorectal cancer.

RETRACTION: Up-regulated Mir-192-5p Expression Rescues Cognitive Impairment and Restores Neural Function in Mice With Depression via the Fbln2 -mediated TGF-β1 Signaling Pathway.

Transferrin-Conjugated Polymeric Nanoparticles via Polymerization-Induced Self-Assembly for Enhanced BBB Transport and Glioblastoma Therapy.

Dasatinib-Loaded Human Serum Albumin Nanoparticle-Impregnated Hydrogel for Localised Eradication of Residual Melanoma: Integrated In Silico, 3D Spheroid, and Dermatokinetic Evaluation.

Therapeutic Advances and Biomarkers in Multiple Sclerosis.

Phospholipid-modified glycogen nanoparticles for synergistic chemo-photothermal treatment of glioblastoma.

Durational Study of Persistent Transduction of Rhesus Macaque Lung and Other Organs Following Single Dosing with AAV1-CFTR.

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A mixed message for cystic fibrosis gene therapy

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