[The liver and gene therapy. Experimental or revolutionary procedure?]

The impact of COVID-19 on rare metabolic patients and healthcare providers: results from two MetabERN surveys.

Orphanet journal of rare diseases·2020

In situ retrovirus-mediated gene transfer into the liver.

Methods in molecular medicine·2014

AAV-mediated delivery of a mutated myostatin propeptide ameliorates calpain 3 but not alpha-sarcoglycan deficiency.

Gene therapy·2007

Enhanced lentiviral transduction of monocyte-derived dendritic cells in the presence of conditioned medium from dying monocytes.

Human gene therapy·2007

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients.

Gene therapy·2006

Synthesis, characterization, and gene transfer application of poly(ethylene glycol-b-ethylenimine) with high molar mass polyamine block.

Biomacromolecules·2006

[In utero treatment of twin-to-twin transfusion syndrome].

La Revue du praticien·2026

[In utero treatment of spina bifida].

La Revue du praticien·2026

[Syphilis and pregnancy].

La Revue du praticien·2026

[Second-line treatments for Parkinson's disease].

La Revue du praticien·2026

[Ageism in healthcare: sad prejudices!]

La Revue du praticien·2026

[Vaccination for pregnant women].

La Revue du praticien·2026

New-Onset Raynaud Phenomenon during Ropeginterferon Alfa-2b Therapy for Polycythemia Vera: A Case Report and Review of the Literature.

Case reports in oncology·2026

131I-labeled engineered hybrid cell membrane biomimetic nanocarrier targets gastric cancer and enhances radioimmunotherapy.

Materials today. Bio·2026

Plant-Derived Extracellular Vesicles Delivered by Microinfusion Microneedling for Androgenetic Alopecia: A Retrospective Case Series.

Skin appendage disorders·2026

Erratum: Brem EA, Shieh K, Juarez D, et al. A phase 1 study adding pitavastatin to venetoclax therapy in AML and CLL/SLL: a mechanism-based drug repurposing strategy. Blood Neoplasia. 2024;1(4):100036.

Blood neoplasia·2026

Machine learning driven precision medicine in tacrolimus dosing: current research and future perspectives in liver and kidney transplantation.

Frontiers in immunology·2026

Modular engineered outer membrane vesicles for synergistic cancer immunotherapy via PD-L1 blockade and epigenetic reprogramming.

Frontiers in immunology·2026

Related Experiment Videos

[The liver and gene therapy. Experimental or revolutionary procedure?]

Related Concept Videos

The impact of COVID-19 on rare metabolic patients and healthcare providers: results from two MetabERN surveys.

In situ retrovirus-mediated gene transfer into the liver.

AAV-mediated delivery of a mutated myostatin propeptide ameliorates calpain 3 but not alpha-sarcoglycan deficiency.

Enhanced lentiviral transduction of monocyte-derived dendritic cells in the presence of conditioned medium from dying monocytes.

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients.

Synthesis, characterization, and gene transfer application of poly(ethylene glycol-b-ethylenimine) with high molar mass polyamine block.

[In utero treatment of twin-to-twin transfusion syndrome].

[In utero treatment of spina bifida].

[Syphilis and pregnancy].

[Second-line treatments for Parkinson's disease].

[Ageism in healthcare: sad prejudices!]

[Vaccination for pregnant women].

New-Onset Raynaud Phenomenon during Ropeginterferon Alfa-2b Therapy for Polycythemia Vera: A Case Report and Review of the Literature.

131I-labeled engineered hybrid cell membrane biomimetic nanocarrier targets gastric cancer and enhances radioimmunotherapy.

Plant-Derived Extracellular Vesicles Delivered by Microinfusion Microneedling for Androgenetic Alopecia: A Retrospective Case Series.

Erratum: Brem EA, Shieh K, Juarez D, et al. A phase 1 study adding pitavastatin to venetoclax therapy in AML and CLL/SLL: a mechanism-based drug repurposing strategy. Blood Neoplasia. 2024;1(4):100036.

Machine learning driven precision medicine in tacrolimus dosing: current research and future perspectives in liver and kidney transplantation.

Modular engineered outer membrane vesicles for synergistic cancer immunotherapy via PD-L1 blockade and epigenetic reprogramming.

Related Experiment Videos

[The liver and gene therapy. Experimental or revolutionary procedure?]

Related Concept Videos

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