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Human Mutation
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April 23, 2013
ANO5 gene analysis in a large cohort of patients with anoctaminopathy: confirmation of male prevalence and high occurrence of the common exon 5 gene mutation
Anna Sarkozy, Debbie Hicks, Judith Hudson, et al.
Brain : a Journal of Neurology
|
September 3, 2020
New genotype-phenotype correlations in a large European cohort of patients with sarcoglycanopathy
Jorge Alonso-Pérez, Lidia González-Quereda, Luca Bello, et al.
Medrxiv : the Preprint Server for Health Sciences
|
April 8, 2024
The recurrent deep intronic pseudoexon-inducing variant <i>COL6A1</i> c.930+189C>T results in a consistently severe phenotype of COL6-related dystrophy: Towards clinical trial readiness for splice-modulating therapy
A Reghan Foley, Véronique Bolduc, Fady Guirguis, et al.
Brain : a Journal of Neurology
|
April 3, 2025
Characterization of severe COL6-related dystrophy due to the recurrent variant COL6A1 c.930+189C>T
A Reghan Foley, Véronique Bolduc, Fady Guirguis, et al.
Brain : a Journal of Neurology
|
July 30, 2023
Neuromuscular disease genetics in under-represented populations: increasing data diversity
Lindsay A Wilson, William L Macken, Luke D Perry, et al.
Nature Genetics
|
March 1, 2024
Digenic inheritance involving a muscle-specific protein kinase and the giant titin protein causes a skeletal muscle myopathy
Ana Töpf, Dan Cox, Irina T Zaharieva, et al.
American Journal of Human Genetics
|
August 2, 2020
De Novo and Bi-allelic Pathogenic Variants in NARS1 Cause Neurodevelopmental Delay Due to Toxic Gain-of-Function and Partial Loss-of-Function Effects
Andreea Manole, Stephanie Efthymiou, Emer O'Connor, et al.
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Search research articles
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Showing results (131-140 of 137) with videos related to
Sort By:
Page
of 14
You have reached the last page of results.
This site can display upto 137 results.
Human Mutation
|
April 23, 2013
ANO5 gene analysis in a large cohort of patients with anoctaminopathy: confirmation of male prevalence and high occurrence of the common exon 5 gene mutation
Anna Sarkozy, Debbie Hicks, Judith Hudson, et al.
Brain : a Journal of Neurology
|
September 3, 2020
New genotype-phenotype correlations in a large European cohort of patients with sarcoglycanopathy
Jorge Alonso-Pérez, Lidia González-Quereda, Luca Bello, et al.
Medrxiv : the Preprint Server for Health Sciences
|
April 8, 2024
The recurrent deep intronic pseudoexon-inducing variant <i>COL6A1</i> c.930+189C>T results in a consistently severe phenotype of COL6-related dystrophy: Towards clinical trial readiness for splice-modulating therapy
A Reghan Foley, Véronique Bolduc, Fady Guirguis, et al.
Brain : a Journal of Neurology
|
April 3, 2025
Characterization of severe COL6-related dystrophy due to the recurrent variant COL6A1 c.930+189C>T
A Reghan Foley, Véronique Bolduc, Fady Guirguis, et al.
Brain : a Journal of Neurology
|
July 30, 2023
Neuromuscular disease genetics in under-represented populations: increasing data diversity
Lindsay A Wilson, William L Macken, Luke D Perry, et al.
Nature Genetics
|
March 1, 2024
Digenic inheritance involving a muscle-specific protein kinase and the giant titin protein causes a skeletal muscle myopathy
Ana Töpf, Dan Cox, Irina T Zaharieva, et al.
American Journal of Human Genetics
|
August 2, 2020
De Novo and Bi-allelic Pathogenic Variants in NARS1 Cause Neurodevelopmental Delay Due to Toxic Gain-of-Function and Partial Loss-of-Function Effects
Andreea Manole, Stephanie Efthymiou, Emer O'Connor, et al.
Page
of 14