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Neurotherapeutics : the Journal of the American Society for Experimental Neurotherapeutics
|
February 24, 2021
Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study
Stacy A Rudnicki, Jinsy A Andrews, Tina Duong, et al.
Neurotherapeutics : the Journal of the American Society for Experimental Neurotherapeutics
|
November 3, 2021
Correction to: Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study
Stacy A Rudnicki, Jinsy A Andrews, Tina Duong, et al.
Neuromuscular Disorders : NMD
|
January 16, 2021
Corrigendum to "Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy" [Neuromuscular Disorders, Vol. 30 (6) 2020, 492-502]
Kathryn R Wagner, Hoda Z Abdel-Hamid, Jean K Mah, et al.
Lancet (London, England)
|
July 22, 2017
Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Craig M McDonald, Craig Campbell, Ricardo Erazo Torricelli, et al.
Muscle & Nerve
|
April 16, 2022
Randomized phase 2 study of ACE-083, a muscle-promoting agent, in facioscapulohumeral muscular dystrophy
Jeffrey M Statland, Craig Campbell, Urvi Desai, et al.
Orphanet Journal of Rare Diseases
|
August 17, 2019
Correction to: Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Libby Wood, Guillaume Bassez, Corinne Bleyenheuft, et al.
Orphanet Journal of Rare Diseases
|
September 7, 2018
Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Libby Wood, Guillaume Bassez, Corinne Bleyenheuft, et al.
Muscle & Nerve
|
July 22, 2014
Ataluren treatment of patients with nonsense mutation dystrophinopathy
Katharine Bushby, Richard Finkel, Brenda Wong, et al.
Journal of Comparative Effectiveness Research
|
August 28, 2020
Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy
Craig Campbell, Richard J Barohn, Enrico Bertini, et al.
The Canadian Journal of Neurological Sciences. Le Journal Canadien Des Sciences Neurologiques
|
June 5, 2020
A National Spinal Muscular Atrophy Registry for Real-World Evidence
Victoria L Hodgkinson, Maryam Oskoui, Joshua Lounsberry, et al.
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of 19
Search research articles
Search
Showing results (171-180 of 188) with videos related to
Sort By:
Page
of 19
Neurotherapeutics : the Journal of the American Society for Experimental Neurotherapeutics
|
February 24, 2021
Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study
Stacy A Rudnicki, Jinsy A Andrews, Tina Duong, et al.
Neurotherapeutics : the Journal of the American Society for Experimental Neurotherapeutics
|
November 3, 2021
Correction to: Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study
Stacy A Rudnicki, Jinsy A Andrews, Tina Duong, et al.
Neuromuscular Disorders : NMD
|
January 16, 2021
Corrigendum to "Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy" [Neuromuscular Disorders, Vol. 30 (6) 2020, 492-502]
Kathryn R Wagner, Hoda Z Abdel-Hamid, Jean K Mah, et al.
Lancet (London, England)
|
July 22, 2017
Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Craig M McDonald, Craig Campbell, Ricardo Erazo Torricelli, et al.
Muscle & Nerve
|
April 16, 2022
Randomized phase 2 study of ACE-083, a muscle-promoting agent, in facioscapulohumeral muscular dystrophy
Jeffrey M Statland, Craig Campbell, Urvi Desai, et al.
Orphanet Journal of Rare Diseases
|
August 17, 2019
Correction to: Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Libby Wood, Guillaume Bassez, Corinne Bleyenheuft, et al.
Orphanet Journal of Rare Diseases
|
September 7, 2018
Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease
Libby Wood, Guillaume Bassez, Corinne Bleyenheuft, et al.
Muscle & Nerve
|
July 22, 2014
Ataluren treatment of patients with nonsense mutation dystrophinopathy
Katharine Bushby, Richard Finkel, Brenda Wong, et al.
Journal of Comparative Effectiveness Research
|
August 28, 2020
Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy
Craig Campbell, Richard J Barohn, Enrico Bertini, et al.
The Canadian Journal of Neurological Sciences. Le Journal Canadien Des Sciences Neurologiques
|
June 5, 2020
A National Spinal Muscular Atrophy Registry for Real-World Evidence
Victoria L Hodgkinson, Maryam Oskoui, Joshua Lounsberry, et al.
Page
of 19