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Frontiers in Pharmacology|November 21, 2022
Selecting the right therapeutic target for kidney diseaseLisa Buvall, Robert I Menzies, Julie Williams, et al.Circulation|March 3, 2010
Protein aggregates and novel presenilin gene variants in idiopathic dilated cardiomyopathyDavide Gianni, Airong Li, Giuseppina Tesco, et al.Basic Research in Cardiology|August 29, 2013
Stanniocalcin1 is a key mediator of amyloidogenic light chain induced cardiotoxicityJian Guan, Shikha Mishra, Jianru Shi, et al.Toxicologic Pathology|February 22, 2024
Adeno-Associated Virus-Mediated Dorsal Root Ganglion Toxicity in the New Zealand White RabbitEric Tien, Branka Grubor, Melissa Kirkland, et al.Cancer Research|October 3, 2007
Depletion of peripheral macrophages and brain microglia increases brain tumor titers of oncolytic virusesGiulia Fulci, Nina Dmitrieva, Davide Gianni, et al.Nature|September 15, 2015
Transcriptional plasticity promotes primary and acquired resistance to BET inhibitionPhilipp Rathert, Mareike Roth, Tobias Neumann, et al.Journal of Molecular Cell Biology|October 14, 2015
Atad2 is a generalist facilitator of chromatin dynamics in embryonic stem cellsYuichi Morozumi, Fayçal Boussouar, Minjia Tan, et al.Journal of Medicinal Chemistry|May 22, 2026
Use of Human Dose Prediction Metrics to Enable Discovery of AZD3470, an MTA-Cooperative PRMT5 Inhibitor in Clinical EvaluationJames M Smith, Bernard Barlaam, David Beattie, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|March 26, 2026
Identification Of a Therapeutic Threshold For AAV-STXBP1 Gene Therapy in a Rodent Model of STXBP1 Developmental & Epileptic EncephalopathyNicholas B Gallo, John W Annand, Pete Clarner, et al.Molecular Therapy. Advances|July 9, 2026
Intra-CNS AAV9-GBA1 delivery yields species and route of administration differences in safety and transgene expressionAna Claudia Amaral, Branka Grubor, Davide Gianni, et al.Pageof 6