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Muscle & Nerve|July 13, 2002
Reliability of hand-held dynamometry in spinal muscular atrophyLuciano Merlini, Elena Stacy Mazzone, Alessandra Solari, et al.Developmental Medicine and Child Neurology|September 21, 2019
Performance of Upper Limb module for Duchenne muscular dystrophyAnna G Mayhew, Giorgia Coratti, Elena Stacy Mazzone, et al.Frontiers in Neurology|August 6, 2024
Long-term efficacy, safety, and patient-reported outcomes of apitegromab in patients with spinal muscular atrophy: results from the 36-month TOPAZ studyThomas O Crawford, John W Day, Darryl C De Vivo, et al.Plos One|August 6, 2016
Revised North Star Ambulatory Assessment for Young Boys with Duchenne Muscular DystrophyEugenio Mercuri, Giorgia Coratti, Sonia Messina, et al.Neuromuscular Disorders : NMD|March 29, 2013
Early neurodevelopmental assessment in Duchenne muscular dystrophyMarika Pane, Roberta Scalise, Angela Berardinelli, et al.The Lancet. Neurology|August 16, 2025
Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trialThomas O Crawford, Laurent Servais, Eugenio Mercuri, et al.Journal of Clinical Medicine|March 11, 2023
2-Year Change in Revised Hammersmith Scale Scores in a Large Cohort of Untreated Paediatric Type 2 and 3 SMA ParticipantsGeorgia Stimpson, Danielle Ramsey, Amy Wolfe, et al.Plos One|January 18, 2013
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophyElena Stacy Mazzone, Marika Pane, Maria Pia Sormani, et al.Neuromuscular Disorders : NMD|January 4, 2022
Revised upper limb module in type II and III spinal muscular atrophy: 24-month changesGiorgia Coratti, Maria Carmela Pera, Jacqueline Montes, et al.Muscle & Nerve|July 30, 2021
Different trajectories in upper limb and gross motor function in spinal muscular atrophyGiorgia Coratti, Maria Carmela Pera, Jacqueline Montes, et al.Pageof 2