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Molecular Therapy. Methods & Clinical Development
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August 28, 2023
Crossing the gates of Babylon: Brain-penetrating enzyme replacement for lysosomal disorders
Guilherme Baldo
Nature Medicine
|
August 19, 2025
Location matters for brain gene therapy in lysosomal disorders
Guilherme Baldo
Progress in Molecular Biology and Translational Science
|
June 15, 2021
Creating cell lines for mimicking diseases
Edina Poletto, Guilherme Baldo
Expert Opinion on Investigational Drugs
|
October 26, 2017
Phase I and II clinical trials for the mucopolysaccharidoses
Fabiano Poswar, Guilherme Baldo, Roberto Giugliani
Medical Hypotheses
|
February 25, 2014
Lysosomal enzymes may cross the blood-brain-barrier by pinocytosis: implications for enzyme replacement therapy
Guilherme Baldo, Roberto Giugliani, Ursula Matte
BMC Medical Genetics
|
October 6, 2018
Comment on "report of 5 novel mutations of the α-L-iduronidase gene and comparison of Korean mutations in relation with those of Japan or China in patients with mucopolysaccharidosis I"
Edina Poletto, Ursula Matte, Guilherme Baldo
Expert Opinion on Drug Delivery
|
January 24, 2014
Gene delivery strategies for the treatment of mucopolysaccharidoses
Guilherme Baldo, Roberto Giugliani, Ursula Matte
International Journal of Molecular Sciences
|
January 17, 2020
Genome Editing for Mucopolysaccharidoses
Edina Poletto, Guilherme Baldo, Natalia Gomez-Ospina
Expert Opinion on Drug Delivery
|
June 21, 2016
Nanotechnology applied to treatment of mucopolysaccharidoses
Roselena S Schuh, Guilherme Baldo, Helder F Teixeira
Frontiers in Genome Editing
|
July 24, 2023
Editorial: <i>Ex-vivo</i> and <i>in-vivo</i> genome engineering for metabolic and neurometabolic diseases
Pasqualina Colella, Vasco Meneghini, Guilherme Baldo, et al.
Page
of 11
Search research articles
Search
Showing results (1-10 of 105) with videos related to
Sort By:
Page
of 11
Molecular Therapy. Methods & Clinical Development
|
August 28, 2023
Crossing the gates of Babylon: Brain-penetrating enzyme replacement for lysosomal disorders
Guilherme Baldo
Nature Medicine
|
August 19, 2025
Location matters for brain gene therapy in lysosomal disorders
Guilherme Baldo
Progress in Molecular Biology and Translational Science
|
June 15, 2021
Creating cell lines for mimicking diseases
Edina Poletto, Guilherme Baldo
Expert Opinion on Investigational Drugs
|
October 26, 2017
Phase I and II clinical trials for the mucopolysaccharidoses
Fabiano Poswar, Guilherme Baldo, Roberto Giugliani
Medical Hypotheses
|
February 25, 2014
Lysosomal enzymes may cross the blood-brain-barrier by pinocytosis: implications for enzyme replacement therapy
Guilherme Baldo, Roberto Giugliani, Ursula Matte
BMC Medical Genetics
|
October 6, 2018
Comment on "report of 5 novel mutations of the α-L-iduronidase gene and comparison of Korean mutations in relation with those of Japan or China in patients with mucopolysaccharidosis I"
Edina Poletto, Ursula Matte, Guilherme Baldo
Expert Opinion on Drug Delivery
|
January 24, 2014
Gene delivery strategies for the treatment of mucopolysaccharidoses
Guilherme Baldo, Roberto Giugliani, Ursula Matte
International Journal of Molecular Sciences
|
January 17, 2020
Genome Editing for Mucopolysaccharidoses
Edina Poletto, Guilherme Baldo, Natalia Gomez-Ospina
Expert Opinion on Drug Delivery
|
June 21, 2016
Nanotechnology applied to treatment of mucopolysaccharidoses
Roselena S Schuh, Guilherme Baldo, Helder F Teixeira
Frontiers in Genome Editing
|
July 24, 2023
Editorial: <i>Ex-vivo</i> and <i>in-vivo</i> genome engineering for metabolic and neurometabolic diseases
Pasqualina Colella, Vasco Meneghini, Guilherme Baldo, et al.
Page
of 11