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Human Gene Therapy Methods
|
July 24, 2018
Standardized Method for Intra-Cisterna Magna Delivery Under Fluoroscopic Guidance in Nonhuman Primates
Nathan Katz, Tamara Goode, Christian Hinderer, et al.
Toxicologic Pathology
|
December 13, 2024
Neuropathological Findings in Nonclinical Species Following Administration of Adeno-Associated Virus (AAV)-Based Gene Therapy Vectors
Brad Bolon, Elizabeth Buza, Elizabeth Galbreath, et al.
Research Square
|
July 18, 2023
Quantification of human mature frataxin protein expression in nonhuman primate hearts after gene therapy
Ian Blair, Teerapat Rojsajjakul, Juliette Hordeaux, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
February 12, 2018
The Neurotropic Properties of AAV-PHP.B Are Limited to C57BL/6J Mice
Juliette Hordeaux, Qiang Wang, Nathan Katz, et al.
Plos One
|
May 16, 2017
Dose escalation study to evaluate safety, tolerability and efficacy of intravenous etoposide phosphate administration in 27 dogs with multicentric lymphoma
Pierre Boyé, François Serres, Laurent Marescaux, et al.
Cerebellum (London, England)
|
February 5, 2025
Functional Characterization of Parallel Fiber-Purkinje Cell Synapses in Two Friedreich's Ataxia Mouse Models
Donald J Joseph, Elizabeth Mercado-Ayon, Liam Flatley, et al.
Molecular Therapy. Methods & Clinical Development
|
August 4, 2018
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques
Juliette Hordeaux, Christian Hinderer, Tamara Goode, et al.
Molecular Therapy. Methods & Clinical Development
|
August 4, 2018
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques
Juliette Hordeaux, Christian Hinderer, Tamara Goode, et al.
Human Gene Therapy
|
April 25, 2019
Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys
Juliette Hordeaux, Christian Hinderer, Elizabeth L Buza, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 2, 2019
The GPI-Linked Protein LY6A Drives AAV-PHP.B Transport across the Blood-Brain Barrier
Juliette Hordeaux, Yuan Yuan, Peter M Clark, et al.
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Search research articles
Search
Showing results (1-10 of 19) with videos related to
Sort By:
Page
of 2
Human Gene Therapy Methods
|
July 24, 2018
Standardized Method for Intra-Cisterna Magna Delivery Under Fluoroscopic Guidance in Nonhuman Primates
Nathan Katz, Tamara Goode, Christian Hinderer, et al.
Toxicologic Pathology
|
December 13, 2024
Neuropathological Findings in Nonclinical Species Following Administration of Adeno-Associated Virus (AAV)-Based Gene Therapy Vectors
Brad Bolon, Elizabeth Buza, Elizabeth Galbreath, et al.
Research Square
|
July 18, 2023
Quantification of human mature frataxin protein expression in nonhuman primate hearts after gene therapy
Ian Blair, Teerapat Rojsajjakul, Juliette Hordeaux, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
February 12, 2018
The Neurotropic Properties of AAV-PHP.B Are Limited to C57BL/6J Mice
Juliette Hordeaux, Qiang Wang, Nathan Katz, et al.
Plos One
|
May 16, 2017
Dose escalation study to evaluate safety, tolerability and efficacy of intravenous etoposide phosphate administration in 27 dogs with multicentric lymphoma
Pierre Boyé, François Serres, Laurent Marescaux, et al.
Cerebellum (London, England)
|
February 5, 2025
Functional Characterization of Parallel Fiber-Purkinje Cell Synapses in Two Friedreich's Ataxia Mouse Models
Donald J Joseph, Elizabeth Mercado-Ayon, Liam Flatley, et al.
Molecular Therapy. Methods & Clinical Development
|
August 4, 2018
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques
Juliette Hordeaux, Christian Hinderer, Tamara Goode, et al.
Molecular Therapy. Methods & Clinical Development
|
August 4, 2018
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques
Juliette Hordeaux, Christian Hinderer, Tamara Goode, et al.
Human Gene Therapy
|
April 25, 2019
Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys
Juliette Hordeaux, Christian Hinderer, Elizabeth L Buza, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 2, 2019
The GPI-Linked Protein LY6A Drives AAV-PHP.B Transport across the Blood-Brain Barrier
Juliette Hordeaux, Yuan Yuan, Peter M Clark, et al.
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of 2