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Current Opinion in Lipidology
|
December 15, 2021
Therapeutic application of genome editing in dyslipidemia
Madelynn N Whittaker, Kiran Musunuru
Science (New York, N.Y.)
|
June 27, 2024
An epigenetic editor to silence genes
Madelynn N Whittaker, Kiran Musunuru
Science (New York, N.Y.)
|
March 29, 2020
Unconstrained genome targeting with near-PAMless engineered CRISPR-Cas9 variants
Russell T Walton, Kathleen A Christie, Madelynn N Whittaker, et al.
American Journal of Human Genetics
|
November 4, 2023
Efficient in vivo prime editing corrects the most frequent phenylketonuria variant, associated with high unmet medical need
Dominique L Brooks, Madelynn N Whittaker, Ping Qu, et al.
HGG Advances
|
November 3, 2023
A base editing strategy using mRNA-LNPs for in vivo correction of the most frequent phenylketonuria variant
Dominique L Brooks, Madelynn N Whittaker, Hooda Said, et al.
Biorxiv : the Preprint Server for Biology
|
June 9, 2023
Epigenome Editing Durability Varies Widely Across Cardiovascular Disease Target Genes
Madelynn N Whittaker, Lauren C Testa, Aidan Quigley, et al.
JCI Insight
|
August 30, 2022
Allele-specific silencing of the gain-of-function mutation in Huntington's disease using CRISPR/Cas9
Jun Wan Shin, Eun Pyo Hong, Seri S Park, et al.
Biorxiv : the Preprint Server for Biology
|
May 7, 2024
Improved specificity and efficacy of base-editing therapies with hybrid guide RNAs
Madelynn N Whittaker, Dominique L Brooks, Aidan Quigley, et al.
American Journal of Human Genetics
|
April 2, 2026
Implications of the FDA's new plausible mechanism framework for the development of a personalized in vivo prime editing platform
Emily R Feierman, Madelynn N Whittaker, Aidan Quigley, et al.
Nature Communications
|
August 15, 2023
Treatment of monogenic and digenic dominant genetic hearing loss by CRISPR-Cas9 ribonucleoprotein delivery in vivo
Yong Tao, Veronica Lamas, Wan Du, et al.
Page
of 2
Search research articles
Search
Showing results (1-10 of 14) with videos related to
Sort By:
Page
of 2
Current Opinion in Lipidology
|
December 15, 2021
Therapeutic application of genome editing in dyslipidemia
Madelynn N Whittaker, Kiran Musunuru
Science (New York, N.Y.)
|
June 27, 2024
An epigenetic editor to silence genes
Madelynn N Whittaker, Kiran Musunuru
Science (New York, N.Y.)
|
March 29, 2020
Unconstrained genome targeting with near-PAMless engineered CRISPR-Cas9 variants
Russell T Walton, Kathleen A Christie, Madelynn N Whittaker, et al.
American Journal of Human Genetics
|
November 4, 2023
Efficient in vivo prime editing corrects the most frequent phenylketonuria variant, associated with high unmet medical need
Dominique L Brooks, Madelynn N Whittaker, Ping Qu, et al.
HGG Advances
|
November 3, 2023
A base editing strategy using mRNA-LNPs for in vivo correction of the most frequent phenylketonuria variant
Dominique L Brooks, Madelynn N Whittaker, Hooda Said, et al.
Biorxiv : the Preprint Server for Biology
|
June 9, 2023
Epigenome Editing Durability Varies Widely Across Cardiovascular Disease Target Genes
Madelynn N Whittaker, Lauren C Testa, Aidan Quigley, et al.
JCI Insight
|
August 30, 2022
Allele-specific silencing of the gain-of-function mutation in Huntington's disease using CRISPR/Cas9
Jun Wan Shin, Eun Pyo Hong, Seri S Park, et al.
Biorxiv : the Preprint Server for Biology
|
May 7, 2024
Improved specificity and efficacy of base-editing therapies with hybrid guide RNAs
Madelynn N Whittaker, Dominique L Brooks, Aidan Quigley, et al.
American Journal of Human Genetics
|
April 2, 2026
Implications of the FDA's new plausible mechanism framework for the development of a personalized in vivo prime editing platform
Emily R Feierman, Madelynn N Whittaker, Aidan Quigley, et al.
Nature Communications
|
August 15, 2023
Treatment of monogenic and digenic dominant genetic hearing loss by CRISPR-Cas9 ribonucleoprotein delivery in vivo
Yong Tao, Veronica Lamas, Wan Du, et al.
Page
of 2