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Medecine Sciences : M/S|January 31, 2025
[A CRISPR/Cas approach to β-haemoglobinopathies]Megane Brusson, Annarita MiccioTrends in Molecular Medicine|January 10, 2025
Gene therapy for β-thalassemia: current and future optionsGiulia Hardouin, Annarita Miccio, Megane BrussonAnnual Review of Pharmacology and Toxicology|September 11, 2024
Treating Sickle Cell Disease: Gene Therapy ApproachesMarina Cavazzana, Alice Corsia, Megane Brusson, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|July 24, 2024
Safety and efficacy studies of CRISPR-Cas9 treatment of sickle cell disease highlights disease-specific responsesGiacomo Frati, Megane Brusson, Gilles Sartre, et al.Trends in Biotechnology|May 22, 2026
CleanFinder: a scalable framework for comprehensive genome editing analysisHaribaskar Ramachandran, Jochen Dobner, Thach Nguyen, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|August 21, 2021
Combination of lentiviral and genome editing technologies for the treatment of sickle cell diseaseSophie Ramadier, Anne Chalumeau, Tristan Felix, et al.Nature Communications|November 5, 2022
Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expressionPanagiotis Antoniou, Giulia Hardouin, Pierre Martinucci, et al.Pageof 1