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Pharmaceutics
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May 27, 2023
Homology-Directed-Repair-Based Genome Editing in HSPCs for the Treatment of Inborn Errors of Immunity and Blood Disorders
Daniel Allen, Nechama Kalter, Michael Rosenberg, et al.
Nucleic Acids Research
|
July 30, 2024
Quantifying allele-specific CRISPR editing activity with CRISPECTOR2.0
Guy Assa, Nechama Kalter, Michael Rosenberg, et al.
Molecular Therapy. Methods & Clinical Development
|
April 14, 2025
Precise measurement of CRISPR genome editing outcomes through single-cell DNA sequencing
Nechama Kalter, Saurabh Gulati, Michael Rosenberg, et al.
Nature Communications
|
October 27, 2023
CRISPR-Cas9 engineering of the RAG2 locus via complete coding sequence replacement for therapeutic applications
Daniel Allen, Orli Knop, Bryan Itkowitz, et al.
Molecular Therapy. Nucleic Acids
|
August 8, 2025
Off-target effects in CRISPR-Cas genome editing for human therapeutics: Progress and challenges
Nechama Kalter, Carla Fuster-García, Alfredo Silva, et al.
Molecular Therapy. Nucleic Acids
|
May 25, 2026
Modeling and correction of SCID-X1 using CRISPR-Cas9 homology-directed repair in human HSPCs
Orli Knop, Nimrod Ben Haim, Nechama Kalter, et al.
Frontiers in Genome Editing
|
November 19, 2025
Proceedings of the second annual meeting of GenE-HumDi (COST Action 21113)
María Ortiz-Bueno, Iris Ramos-Hernández, Luis Algeciras-Jiménez, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 11, 2025
Gene-corrected regulatory T cell therapy for IL2RA deficiency
Alvin S Ha, Nechama Kalter, Michael Rosenberg, et al.
Biorxiv : the Preprint Server for Biology
|
May 4, 2026
Development of a Fully Non-Viral 1XX-enhanced BCMA CAR-T Cell Therapy for Multiple Myeloma
Alexis Talbot, Ke Li, Jae Hyun J Lee, et al.
Molecular Therapy. Nucleic Acids
|
November 30, 2023
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi
Alessia Cavazza, Ayal Hendel, Rasmus O Bak, et al.
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Search research articles
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Showing results (1-10 of 10) with videos related to
Sort By:
Page
of 1
Pharmaceutics
|
May 27, 2023
Homology-Directed-Repair-Based Genome Editing in HSPCs for the Treatment of Inborn Errors of Immunity and Blood Disorders
Daniel Allen, Nechama Kalter, Michael Rosenberg, et al.
Nucleic Acids Research
|
July 30, 2024
Quantifying allele-specific CRISPR editing activity with CRISPECTOR2.0
Guy Assa, Nechama Kalter, Michael Rosenberg, et al.
Molecular Therapy. Methods & Clinical Development
|
April 14, 2025
Precise measurement of CRISPR genome editing outcomes through single-cell DNA sequencing
Nechama Kalter, Saurabh Gulati, Michael Rosenberg, et al.
Nature Communications
|
October 27, 2023
CRISPR-Cas9 engineering of the RAG2 locus via complete coding sequence replacement for therapeutic applications
Daniel Allen, Orli Knop, Bryan Itkowitz, et al.
Molecular Therapy. Nucleic Acids
|
August 8, 2025
Off-target effects in CRISPR-Cas genome editing for human therapeutics: Progress and challenges
Nechama Kalter, Carla Fuster-García, Alfredo Silva, et al.
Molecular Therapy. Nucleic Acids
|
May 25, 2026
Modeling and correction of SCID-X1 using CRISPR-Cas9 homology-directed repair in human HSPCs
Orli Knop, Nimrod Ben Haim, Nechama Kalter, et al.
Frontiers in Genome Editing
|
November 19, 2025
Proceedings of the second annual meeting of GenE-HumDi (COST Action 21113)
María Ortiz-Bueno, Iris Ramos-Hernández, Luis Algeciras-Jiménez, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 11, 2025
Gene-corrected regulatory T cell therapy for IL2RA deficiency
Alvin S Ha, Nechama Kalter, Michael Rosenberg, et al.
Biorxiv : the Preprint Server for Biology
|
May 4, 2026
Development of a Fully Non-Viral 1XX-enhanced BCMA CAR-T Cell Therapy for Multiple Myeloma
Alexis Talbot, Ke Li, Jae Hyun J Lee, et al.
Molecular Therapy. Nucleic Acids
|
November 30, 2023
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi
Alessia Cavazza, Ayal Hendel, Rasmus O Bak, et al.
Page
of 1