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Nature Medicine
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February 3, 2026
High-dose nusinersen for spinal muscular atrophy: a phase 3 randomized trial
Richard S Finkel, Thomas O Crawford, Eugenio Mercuri, et al.
Plos One
|
May 15, 2009
Phase II open label study of valproic acid in spinal muscular atrophy
Kathryn J Swoboda, Charles B Scott, Sandra P Reyna, et al.
Brain : a Journal of Neurology
|
February 5, 2013
A novel syndrome caused by the E410K amino acid substitution in the neuronal β-tubulin isotype 3
Sheena Chew, Ravikumar Balasubramanian, Wai-Man Chan, et al.
Plos One
|
July 15, 2011
SMA CARNIVAL TRIAL PART II: a prospective, single-armed trial of L-carnitine and valproic acid in ambulatory children with spinal muscular atrophy
John T Kissel, Charles B Scott, Sandra P Reyna, et al.
Journal of Neuromuscular Diseases
|
December 30, 2025
New SMA era: A broad-range tiered assessment of function for the evolving SMA phenotype (EVOLVE-SMA)
Meghan Moore Burk, Thomas O Crawford, Kristen Johnson, et al.
Journal of Neuromuscular Diseases
|
March 13, 2023
Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambulatory Patients with Spinal Muscular Atrophy: Phase I Ascending-Dose Study (STRONG)
Richard S Finkel, Basil T Darras, Jerry R Mendell, et al.
Muscle & Nerve
|
May 18, 2013
SMA valiant trial: a prospective, double-blind, placebo-controlled trial of valproic acid in ambulatory adults with spinal muscular atrophy
John T Kissel, Bakri Elsheikh, Wendy M King, et al.
Muscle & Nerve
|
June 16, 2026
Electrodiagnostic Studies as a Diagnostic and Prognostic Tool in Acute Flaccid Myelitis
Jelte Helfferich, Judith M Vonk, Melodie Aubart, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
September 3, 2010
Carrier testing for spinal muscular atrophy
Jonathan M Gitlin, Kenneth Fischbeck, Thomas O Crawford, et al.
Brain : a Journal of Neurology
|
June 25, 2024
TRPV4 neuromuscular disease registry highlights bulbar, skeletal and proximal limb manifestations
Gage P Kosmanopoulos, Jack K Donohue, Maya Hoke, et al.
Page
of 19
Search research articles
Search
Showing results (161-170 of 190) with videos related to
Sort By:
Page
of 19
Nature Medicine
|
February 3, 2026
High-dose nusinersen for spinal muscular atrophy: a phase 3 randomized trial
Richard S Finkel, Thomas O Crawford, Eugenio Mercuri, et al.
Plos One
|
May 15, 2009
Phase II open label study of valproic acid in spinal muscular atrophy
Kathryn J Swoboda, Charles B Scott, Sandra P Reyna, et al.
Brain : a Journal of Neurology
|
February 5, 2013
A novel syndrome caused by the E410K amino acid substitution in the neuronal β-tubulin isotype 3
Sheena Chew, Ravikumar Balasubramanian, Wai-Man Chan, et al.
Plos One
|
July 15, 2011
SMA CARNIVAL TRIAL PART II: a prospective, single-armed trial of L-carnitine and valproic acid in ambulatory children with spinal muscular atrophy
John T Kissel, Charles B Scott, Sandra P Reyna, et al.
Journal of Neuromuscular Diseases
|
December 30, 2025
New SMA era: A broad-range tiered assessment of function for the evolving SMA phenotype (EVOLVE-SMA)
Meghan Moore Burk, Thomas O Crawford, Kristen Johnson, et al.
Journal of Neuromuscular Diseases
|
March 13, 2023
Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambulatory Patients with Spinal Muscular Atrophy: Phase I Ascending-Dose Study (STRONG)
Richard S Finkel, Basil T Darras, Jerry R Mendell, et al.
Muscle & Nerve
|
May 18, 2013
SMA valiant trial: a prospective, double-blind, placebo-controlled trial of valproic acid in ambulatory adults with spinal muscular atrophy
John T Kissel, Bakri Elsheikh, Wendy M King, et al.
Muscle & Nerve
|
June 16, 2026
Electrodiagnostic Studies as a Diagnostic and Prognostic Tool in Acute Flaccid Myelitis
Jelte Helfferich, Judith M Vonk, Melodie Aubart, et al.
Genetics in Medicine : Official Journal of the American College of Medical Genetics
|
September 3, 2010
Carrier testing for spinal muscular atrophy
Jonathan M Gitlin, Kenneth Fischbeck, Thomas O Crawford, et al.
Brain : a Journal of Neurology
|
June 25, 2024
TRPV4 neuromuscular disease registry highlights bulbar, skeletal and proximal limb manifestations
Gage P Kosmanopoulos, Jack K Donohue, Maya Hoke, et al.
Page
of 19