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Human Gene Therapy|April 2, 2015
Gene therapy for inherited diseases of liver metabolismPasquale Piccolo, Nicola Brunetti-PierriHuman Gene Therapy|December 23, 2024
Current and Emerging Issues in Adeno-Associated Virus Vector-Mediated Liver-Directed Gene TherapyPasquale Piccolo, Nicola Brunetti-PierriBiomedicines|May 27, 2017
Challenges and Prospects for Helper-Dependent Adenoviral Vector-Mediated Gene TherapyPasquale Piccolo, Nicola Brunetti-PierriCurrent Opinion in Gastroenterology|January 31, 2022
Cholangiopathies and the noncoding revolutionSergio Gradilone, Nicola Brunetti-Pierri, Pasquale PiccoloExpert Opinion on Biological Therapy|September 4, 2020
Liver-directed gene-based therapies for inborn errors of metabolismPasquale Piccolo, Alessandro Rossi, Nicola Brunetti-PierriHuman Gene Therapy|December 24, 2010
Intrathecal injection of helper-dependent adenoviral vectors results in long-term transgene expression in neuroependymal cells and neuronsScott Dindot, Pasquale Piccolo, Nathan Grove, et al.Circulation. Cardiovascular Genetics|December 20, 2012
Supravalvular aortic stenosis: elastin arteriopathyGiuseppe Merla, Nicola Brunetti-Pierri, Pasquale Piccolo, et al.Italian Journal of Pediatrics|June 4, 2009
Gene therapy for inborn errors of liver metabolism: progress towards clinical applicationsNicola Brunetti-PierriMolecular Therapy : the Journal of the American Society of Gene Therapy|January 30, 2013
SR-A and SREC-I are Kupffer and endothelial cell receptors for helper-dependent adenoviral vectorsPasquale Piccolo, Francesco Vetrini, Pratibha Mithbaokar, et al.Molecular Genetics & Genomic Medicine|July 28, 2019
Skin fibroblasts of patients with geleophysic dysplasia due to FBN1 mutations have lysosomal inclusions and losartan improves their microfibril deposition defectPasquale Piccolo, Valeria Sabatino, Pratibha Mithbaokar, et al.Pageof 25