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Ralph D Hector

Showing results (11-20 of 24) with videos related to

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Nature|October 12, 2017
Radically truncated MeCP2 rescues Rett syndrome-like neurological defectsRebekah Tillotson, Jim Selfridge, Martha V Koerner, et al.
Molecular Therapy. Methods & Clinical Development|May 13, 2017
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett SyndromeKamal K E Gadalla, Thishnapha Vudhironarit, Ralph D Hector, et al.
Molecular Therapy. Nucleic Acids|August 28, 2023
Long-term muscle-specific overexpression of DOK7 in mice using AAV9-tMCK-DOK7Yu-Ting Huang, Hannah R Crick, Helena Chaytow, et al.
Molecular Therapy. Methods & Clinical Development|May 13, 2017
Improved <i>MECP2</i> Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal DeliverySarah E Sinnett, Ralph D Hector, Kamal K E Gadalla, et al.
Proceedings of the National Academy of Sciences of the United States of America|November 24, 2011
High-resolution human cytomegalovirus transcriptomeDerek Gatherer, Sepehr Seirafian, Charles Cunningham, et al.
Neurology. Genetics|December 22, 2017
<i>CDKL5</i> variants: Improving our understanding of a rare neurologic disorderRalph D Hector, Vera M Kalscheuer, Friederike Hennig, et al.
Nature Communications|September 30, 2017
High-throughput RNA structure probing reveals critical folding events during early 60S ribosome assembly in yeastElena Burlacu, Fredrik Lackmann, Lisbeth-Carolina Aguilar, et al.
Science Translational Medicine|April 2, 2025
Self-regulating gene therapy ameliorates phenotypes and overcomes gene dosage sensitivity in a mouse model of Rett syndromePaul D Ross, Kamal K E Gadalla, Sophie R Thomson, et al.
Molecular Therapy. Nucleic Acids|July 2, 2026
Neonatal expression of human FMRP isoform corrects cortical deficits and improves behavior in a mouse model of fragile X syndromeAnna O Norman, Courtney Scaramella, Dominik Biezonski, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 2, 2009
A novel model of SCID-X1 reconstitution reveals predisposition to retrovirus-induced lymphoma but no evidence of gammaC gene oncogenicityLinda Scobie, Ralph D Hector, Louise Grant, et al.
Pageof 3

Showing results (11-20 of 24) with videos related to

Sort By:
Pageof 3
Nature|October 12, 2017
Radically truncated MeCP2 rescues Rett syndrome-like neurological defectsRebekah Tillotson, Jim Selfridge, Martha V Koerner, et al.
Molecular Therapy. Methods & Clinical Development|May 13, 2017
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett SyndromeKamal K E Gadalla, Thishnapha Vudhironarit, Ralph D Hector, et al.
Molecular Therapy. Nucleic Acids|August 28, 2023
Long-term muscle-specific overexpression of DOK7 in mice using AAV9-tMCK-DOK7Yu-Ting Huang, Hannah R Crick, Helena Chaytow, et al.
Molecular Therapy. Methods & Clinical Development|May 13, 2017
Improved <i>MECP2</i> Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal DeliverySarah E Sinnett, Ralph D Hector, Kamal K E Gadalla, et al.
Proceedings of the National Academy of Sciences of the United States of America|November 24, 2011
High-resolution human cytomegalovirus transcriptomeDerek Gatherer, Sepehr Seirafian, Charles Cunningham, et al.
Neurology. Genetics|December 22, 2017
<i>CDKL5</i> variants: Improving our understanding of a rare neurologic disorderRalph D Hector, Vera M Kalscheuer, Friederike Hennig, et al.
Nature Communications|September 30, 2017
High-throughput RNA structure probing reveals critical folding events during early 60S ribosome assembly in yeastElena Burlacu, Fredrik Lackmann, Lisbeth-Carolina Aguilar, et al.
Science Translational Medicine|April 2, 2025
Self-regulating gene therapy ameliorates phenotypes and overcomes gene dosage sensitivity in a mouse model of Rett syndromePaul D Ross, Kamal K E Gadalla, Sophie R Thomson, et al.
Molecular Therapy. Nucleic Acids|July 2, 2026
Neonatal expression of human FMRP isoform corrects cortical deficits and improves behavior in a mouse model of fragile X syndromeAnna O Norman, Courtney Scaramella, Dominik Biezonski, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 2, 2009
A novel model of SCID-X1 reconstitution reveals predisposition to retrovirus-induced lymphoma but no evidence of gammaC gene oncogenicityLinda Scobie, Ralph D Hector, Louise Grant, et al.
Pageof 3