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Methods in Molecular Biology (Clifton, N.J.)|February 25, 2022
Antisense RNA Therapeutics: A Brief OverviewVirginia Arechavala-Gomeza, Alejandro Garanto
Genes|February 11, 2021
Special Issue "Genetic Advances in Neuromuscular Disorders: From Gene Identification to Gene Therapy"Virginia Arechavala-Gomeza, Lidia Gonzalez-Quereda
Nucleic Acid Therapeutics|May 5, 2023
Experimental Model Systems Used in the Preclinical Development of Nucleic Acid TherapeuticsHaiyan Zhou, Virginia Arechavala-Gomeza, Alejandro Garanto
Nucleic Acid Therapeutics|July 31, 2020
Researcher's Perceptions on Publishing "Negative" Results and Open AccessLucía Echevarría, Alberto Malerba, Virginia Arechavala-Gomeza
The Application of Clinical Genetics|December 16, 2014
Splicing modulation therapy in the treatment of genetic diseasesVirginia Arechavala-Gomeza, Bernard Khoo, Annemieke Aartsma-Rus
Current Gene Therapy|April 27, 2012
Antisense oligonucleotide-mediated exon skipping for Duchenne muscular dystrophy: progress and challengesVirginia Arechavala-Gomeza, Karen Anthony, Jennifer Morgan, et al.
Methods in Molecular Biology (Clifton, N.J.)|February 25, 2022
Evaluation of Exon Skipping and Dystrophin Restoration in In Vitro Models of Duchenne Muscular DystrophyAndrea López-Martínez, Patricia Soblechero-Martín, Virginia Arechavala-Gomeza
Journal of Neuromuscular Diseases|March 28, 2025
Antisense RNA therapies for muscular dystrophiesVirginia Arechavala-Gomeza, Andrea López-Martínez, Annemieke Aartsma-Rus
Journal of Clinical Medicine|December 9, 2020
The Biomarker Potential of miRNAs in Myotonic Dystrophy Type IEmma Koehorst, Alfonsina Ballester-Lopez, Virginia Arechavala-Gomeza, et al.
Neuromuscular Disorders : NMD|December 26, 2009
The contribution of human synovial stem cells to skeletal muscle regenerationJinhong Meng, Carl F Adkin, Virginia Arechavala-Gomeza, et al.
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