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Human Gene Therapy|June 13, 2015
Delivery and Specificity of CRISPR-Cas9 Genome Editing Technologies for Human Gene TherapyJennifer L Gori, Patrick D Hsu, Morgan L Maeder, et al.Human Gene Therapy|June 19, 2015
Adenovirus-Mediated Somatic Genome Editing of Pten by CRISPR/Cas9 in Mouse Liver in Spite of Cas9-Specific Immune ResponsesDan Wang, Haiwei Mou, Shaoyong Li, et al.Human Gene Therapy|February 8, 2018
Hepatocyte Growth Factor Gene Therapy for Ischemic DiseasesLi-Sheng Wang, Hua Wang, Qing-Lin Zhang, et al.Human Gene Therapy|February 8, 2018
Therapeutic Potential of Lentivirus-Mediated Glucagon-Like Peptide-1 Gene Therapy for DiabetesHale M Tasyurek, Hasan Ali Altunbas, Mustafa Kemal Balci, et al.Human Gene Therapy|January 24, 2018
Recent Progress on Genetic Diagnosis and Therapy for β-Thalassemia in China and Around the WorldJingzhi Zhang, Jingbin Yan, Fanyi ZengHuman Gene Therapy|January 12, 2018
Chimeric Antigen Receptors in Different Cell Types: New Vehicles Join the RaceDennis C Harrer, Jan Dörrie, Niels SchaftHuman Gene Therapy|March 28, 2018
Assessment of AAV Vector Tropisms for Mouse and Human Pluripotent Stem Cell-Derived RPE and Photoreceptor CellsAnai Gonzalez-Cordero, Debbie Goh, Kamil Kruczek, et al.Human Gene Therapy|January 17, 2018
MACF1 Overexpression by Transfecting the 21 kbp Large Plasmid PEGFP-C1A-ACF7 Promotes Osteoblast Differentiation and Bone FormationYan Zhang, Chong Yin, Lifang Hu, et al.Human Gene Therapy|January 28, 2018
Third-Generation Human Epidermal Growth Factor Receptor 2 Chimeric Antigen Receptor Expression on Human T Cells Improves with Two-Signal ActivationAl-Rubaye Dalal, Sylvester Homsy, Mumtaz Y BalkhiHuman Gene Therapy|March 31, 2018
In Vivo Genome Editing Partially Restores Alpha1-Antitrypsin in a Murine Model of AAT DeficiencyChun-Qing Song, Dan Wang, Tingting Jiang, et al.Pageof 413