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Charles P Venditti

21PUBLICATIONS

40CO-AUTHORS

Neurology and neuromuscular diseasesCellular nervous systemGene and molecular therapyInfant and child healthMedical biochemistry - amino acids and metabolites

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Publications (21)

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|Mar 30, 2026

Optimization of systemic AAV9 gene therapy in Niemann-Pick disease, type C1 mice.

Avani V Mylvara, Alana L Gibson, Tansy Gu

|Feb 27, 2025

Prevalence of Neutralizing Antibodies to AAV2 and AAV9 in Individuals with Niemann-Pick Disease, Type C1.

Avani V Mylvara, Cristin D Davidson, Derek Alexander

|Feb 20, 2025

Adeno-Associated Virus Gene Therapy Development: Early Planning and Regulatory Considerations to Advance the Platform Vector Gene Therapy Program.

Richa Madan Lomash, Jean Dehdashti, Oleg A Shchelochkov

|Jun 19, 2024

Optimization of systemic AAV9 gene therapy in Niemann-Pick disease type C1 mice.

Avani V Mylvara, Alana L Gibson, Tansy Gu

|Jan 10, 2024

Intellectual disability and autism in propionic acidemia: a biomarker-behavioral investigation implicating dysregulated mitochondrial biology.

Oleg A Shchelochkov, Cristan A Farmer, Colby Chlebowski

|Aug 02, 2023

Gene therapy for organic acidemias: Lessons learned from methylmalonic and propionic acidemia.

Randy J Chandler, Charles P Venditti

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Frequent Collaborators

5 joint publications

Irini Manoli

4 joint publications

Cristin D Davidson

3 joint publications

Avani V Mylvara

3 joint publications

Forbes D Porter

3 joint publications

PamelaSara E Head

3 joint publications

Alana L Gibson

3 joint publications

William J Pavan

2 joint publications

Richa Madan Lomash

2 joint publications

Tansy Gu

2 joint publications

Randy J Chandler

Frequent Collaborators

5 joint publications

Irini Manoli

4 joint publications

Cristin D Davidson

3 joint publications

Avani V Mylvara

3 joint publications

Forbes D Porter

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