William J Pavan
11PUBLICATIONS
38CO-AUTHORS
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Publications (11)
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|Mar 30, 2026
Optimization of systemic AAV9 gene therapy in Niemann-Pick disease, type C1 mice.Avani V Mylvara, Alana L Gibson, Tansy Gu
|Mar 11, 2026
Comparison of neonatal systemic and intracerebroventricular AAV9 gene therapy delivery demonstrating improved behavioral and phenotypic outcomes in a mouse model of Niemann-Pick disease, type C1.Benjamin E Epstein, Gabrielle M Soden, Arturo A Incao
|Jun 19, 2024
Optimization of systemic AAV9 gene therapy in Niemann-Pick disease type C1 mice.Avani V Mylvara, Alana L Gibson, Tansy Gu
|Nov 16, 2023
Single-cell profiling of MC1R-inhibited melanocytes.H Matthew Berns, Dawn E Watkins-Chow, Sizhu Lu
|Feb 10, 2022
Correlation of age of onset and clinical severity in Niemann-Pick disease type C1 with lysosomal abnormalities and gene expression.Laura L Baxter, Dawn E Watkins-Chow, Nicholas L Johnson
|Aug 19, 2021
Improved systemic AAV gene therapy with a neurotrophic capsid in Niemann-Pick disease type C1 mice.Cristin D Davidson, Alana L Gibson, Tansy Gu
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Frequent Collaborators
3 joint publications
Dawn E Watkins-Chow
3 joint publications
Charles P Venditti
3 joint publications
Alana L Gibson
3 joint publications
Cristin D Davidson
3 joint publications
Forbes D Porter
3 joint publications
Jorge L Rodriguez-Gil
2 joint publications
Arturo A Incao
2 joint publications
Avani V Mylvara
2 joint publications
Shawn M Burgess
2 joint publications
Tansy Gu
