Anastasia Khvorova

38PUBLICATIONS
155CO-AUTHORS
Cardiology (incl. cardiovascular diseases)Gene and molecular therapyEpigenetics (incl. genome methylation and epigenomics)Cancer geneticsMicro-manipulation
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Publications (38)

|Aug 12, 2026
Blocking somatic repeat expansion and lowering huntingtin by RNAi synergize to attenuate Huntington's disease pathogenesis in mice.

|Jul 21, 2026
Single-dose administration of therapeutic divalent siRNA targeting MECP2 prevents lethality in an MECP2 duplication mouse model.

|Jul 03, 2026
Mismatch repair dissection by in vivo RNAi reveals dose-dependent modulators of somatic instability and proteome remodeling in Huntington's disease.

|Jun 29, 2026
Precision RNAi for Fibrodysplasia Ossificans Progressiva: a combinatorial, unimolecular, allele selective approach.

|Jun 05, 2026
Fully Modified SpyCas9 Guide RNAs Enable Robust Genome Editing In Cells and In Vivo.

|May 25, 2026
C57BL/6 BAC-CAG Huntington's disease mice show somatic CAG expansion and responses to small interfering RNAs comparable to the FVB strain.

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Frequent Collaborators

16 joint publications

Julia F Alterman

14 joint publications

Dimas Echeverria Moreno

12 joint publications

Ken Yamada

9 joint publications

Ashley Summers