Haydar Frangoul

8PUBLICATIONS
10CO-AUTHORS
HaematologyGene and molecular therapyRegenerative medicine (incl. stem cells)Medical infection agents (incl. prions)Respiratory diseases
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Publications (8)

|Jun 11, 2026
Exa-cel in Children with Transfusion-Dependent β-Thalassemia or Sickle Cell Disease.

|Apr 03, 2026
CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat β-Thalassemia.

Haydar Frangoul, Rabi Hanna, Mark C Walters

|Apr 03, 2026
CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease.

Rabi Hanna, Haydar Frangoul, Luis Pineiro

|Apr 03, 2026
Base Editing of HBG1 and HBG2 Promoters for Sickle Cell Disease.

Ashish O Gupta, Akshay Sharma, Haydar Frangoul

|Dec 08, 2025
Prime Editing for p47phox-Deficient Chronic Granulomatous Disease.

Jennifer L Gori, Elie Haddad, Haydar Frangoul

|Mar 27, 2025
Impact of Different Definitions of Vaso-Occlusion on Efficacy Assessments in Sickle Cell Disease Clinical Trials.

Haydar Frangoul, Franco Locatelli, Michael J Eckrich

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Frequent Collaborators

4 joint publications

Akshay Sharma

3 joint publications

Franco Locatelli

3 joint publications

Selim Corbacioglu

3 joint publications

Mark C Walters