Mark Walters

17PUBLICATIONS
59CO-AUTHORS
Gene and molecular therapyRecommender systemsRegenerative medicine (incl. stem cells)Tissue engineeringCardiology (incl. cardiovascular diseases)
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Publications (17)

|Apr 06, 2026
Cure Sickle Cell Initiative recommendations on common data elements for sickle cell disease gene therapy trials.

Sophie Lanzkron, Victoria H Coleman-Cowger, Alexis A Thompson

|Apr 03, 2026
CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat β-Thalassemia.

Haydar Frangoul, Rabi Hanna, Mark C Walters

|Apr 03, 2026
CRISPR-Cas12a Gene Editing of HBG1 and HBG2 Promoters to Treat Sickle Cell Disease.

Rabi Hanna, Haydar Frangoul, Luis Pineiro

|Mar 26, 2026
A blueprint to accelerate rare pediatric gene therapy approvals.

Mohamed Abou-El-Enein, Mark C Walters, Darshak Sanghavi

|Jan 12, 2026
Long-term efficacy and safety results of betibeglogene autotemcel gene therapy for transfusion-dependent β-thalassemia.

Janet L Kwiatkowski, Alexis A Thompson, Jennifer Schneiderman

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