Annarita Miccio

17PUBLICATIONS
77CO-AUTHORS
HaematologyGene and molecular therapyCellular nervous systemMedical devicesAutomated software engineering
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Publications (17)

|Apr 08, 2026
Clinical application of base editing for treating β-thalassaemia.

Yongrong Lai, Rongrong Liu, Lijie Wang

|Nov 26, 2025
Base editing of β0-thalassemia mutations as a therapeutic strategy for severe β-hemoglobinopathies.

Giulia Hardouin, Pierre Martinucci, Samantha Scaramuzza

|Jan 31, 2025
[A CRISPR/Cas approach to β-haemoglobinopathies].

Megane Brusson, Annarita Miccio

|Nov 02, 2024
Human iPSC-derived neural stem cells displaying radial glia signature exhibit long-term safety in mice.

Marco Luciani, Chiara Garsia, Stefano Beretta

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