Fulvio Mavilio
7PUBLICATIONS
31CO-AUTHORS
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Publications (7)
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|Apr 01, 2025
Severe inflammation and lineage skewing are associated with poor engraftment of engineered hematopoietic stem cells in patients with sickle cell disease.Steicy Sobrino, Laure Joseph, Elisa Magrin
|Dec 01, 2021
Muscle-directed gene therapy corrects Pompe disease and uncovers species-specific GAA immunogenicity.Michelle Eggers, Charles H Vannoy, Jianyong Huang
|Aug 28, 2021
Designing Lentiviral Vectors for Gene Therapy of Genetic Diseases.Valentina Poletti, Fulvio Mavilio
|Sep 12, 2020
Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype.Leslie Weber, Giacomo Frati, Tristan Felix
|Mar 10, 2018
Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus.Chiara Antoniani, Vasco Meneghini, Annalisa Lattanzi
|Jul 26, 2017
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy.Caroline Le Guiner, Laurent Servais, Marie Montus
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Frequent Collaborators
3 joint publications
Tristan Felix
3 joint publications
Annarita Miccio
3 joint publications
Marina Cavazzana
2 joint publications
Mario Amendola
2 joint publications
Wassim El Nemer
1 joint publications
Thibaut Larcher
1 joint publications
Vasco Meneghini
1 joint publications
Annalisa Lattanzi
1 joint publications
Oriana Romano
1 joint publications
Elisa Magrin
