Pasqualina Colella

8PUBLICATIONS
33CO-AUTHORS
MechanobiologyMedical biochemistry - proteins and peptides (incl. medical proteomics)Regenerative medicine (incl. stem cells)Medical molecular engineering of nucleic acids and proteinsMedical devices
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Publications (8)

|Sep 15, 2026
Myeloid cell replacement induces intercellular mitochondrial transfer and restores metabolism in a mouse model of mitochondrial disease.

|Aug 12, 2024
Advances in Pompe Disease Treatment: From Enzyme Replacement to Gene Therapy.

Pasqualina Colella

|Jul 05, 2024
CNS-wide repopulation by hematopoietic-derived microglia-like cells corrects progranulin deficiency in mice.

Pasqualina Colella, Ruhi Sayana, Maria Valentina Suarez-Nieto

|Jun 07, 2022
Neonatal gene therapy achieves sustained disease rescue of maple syrup urine disease in mice.

Clément Pontoizeau, Marcelo Simon-Sola, Clovis Gaborit

|Nov 05, 2021
Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates.

Helena Costa-Verdera, Fanny Collaud, Christopher R Riling

|Aug 22, 2020
Author Correction: Engineering monocyte/macrophage-specific glucocerebrosidase expression in human hematopoietic stem cells using genome editing.

Samantha G Scharenberg, Edina Poletto, Katherine L Lucot

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Frequent Collaborators

4 joint publications

Natalia Gomez-Ospina

2 joint publications

Matthew H Porteus

2 joint publications

Katherine L Lucot

2 joint publications

Giuseppe Ronzitti