Giuseppe Ronzitti

11PUBLICATIONS
75CO-AUTHORS
Gene and molecular therapyInfant and child healthAgricultural molecular engineering of nucleic acids and proteinsPacific Peoples and disabilityMolecular targets
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Publications (11)

|Apr 18, 2025
AAV vectors trigger DNA damage response-dependent pro-inflammatory signalling in human iPSC-derived CNS models and mouse brain.

Helena Costa-Verdera, Vasco Meneghini, Zachary Fitzpatrick

|Apr 11, 2025
Rescue of lysosomal acid lipase deficiency in mice by rAAV8 liver gene transfer.

Marine Laurent, Rim Harb, Christine Jenny

|Mar 11, 2025
Liver fibrosis negatively impacts in vivo gene transfer to murine hepatocytes.

Chiara Simoni, Justine Nozi, Francesco Starinieri

|May 19, 2023
Muscle-specific, liver-detargeted adeno-associated virus gene therapy rescues Pompe phenotype in adult and neonate Gaa-/- mice.

P Sellier, P Vidal, B Bertin

|Feb 06, 2023
LSD1/PRMT6-targeting gene therapy to attenuate androgen receptor toxic gain-of-function ameliorates spinobulbar muscular atrophy phenotypes in flies and mice.

Ramachandran Prakasam, Angela Bonadiman, Roberta Andreotti

|Dec 29, 2022
What's next in gene therapy for Crigler-Najjar syndrome?

Sem J Aronson, Giuseppe Ronzitti, Piter J Bosma

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Frequent Collaborators

4 joint publications

Federico Mingozzi

2 joint publications

Pasqualina Colella

2 joint publications

Helena Costa-Verdera

2 joint publications

Christian Leborgne